Researcher
Ermira Samara
- Keywords:Medicine
Affiliations
- Division of Gene Therapy & Regenerative Medicine (Research group)
Member
From19 Apr 2011 → Today - Medicine and Pharmacy academic/administration (Office)
Member
From1 Jan 2018 → Today - Medicine and Pharmacy academic/administration (Office)
Member
From1 Jan 2014 → 31 Dec 2017 - Cell Biology and Histology (Department)
Member
From1 Dec 2010 → 31 Dec 2013 - Cell Biology and Histology (Department)
Member
From1 Sep 2010 → 31 Aug 2011
Publications
1 - 6 of 6
- Efficient CRISPR/Cas9-mediated editing of trinucleotide repeat expansion in myotonic dystrophy patient-derived iPS and myogenic cells(2018)
Authors: Sumitava Dastidar, Simon Ardui, Kshitiz Singh, Debanjana Majumdar, Nisha Nair, Yanfang Fu, Deepak Reyon, Ermira Samara, Mattia FM Gerbil, Arnaud F. Klein, et al.
Pages: 8275-8298 - Efficient In Vivo Liver-Directed Gene Editing Using CRISPR/Cas9(2018)
Authors: Kshitiz Singh, Hanneke Evens, Nisha Nair, Melvin Rincon Acelas, Shilpita Sarcar, Ermira Samara, Marinee K Chuah, Thierry VandenDriessche
Pages: 1241-1254 - Genome-Wide Computational Analysis Reveals Cardiomyocyte-Specific Transcriptional CIS-Regulatory Motifs that Enable Efficient Cardiac Gene Therapy.(2015)
Authors: Melvin Rincon Acelas, Shilpita Sarcar, D. Danso-Abeam, Marleen Keyaerts, Janka Matrai, Ermira Samara, Abel Acosta-Sanchez, T. Athanasopoulos, G. Dickson, Tony Lahoutte, et al.
Pages: 43-52 - Computationally designed liver-specific transcriptional cis-regulatory modules and hyper-functional factor IX improve liver-targeted gene therapy for hemophilia B.(2014)
Authors: Nisha Nair, M.y. Rincon, Hanneke Evens, Shilpita Sarcar, Ermira Samara, O. Ghandeharian, H. Viecelli, B. Thony, Pieter De Bleser
Pages: 3195-3199 - Hyperactive PIGGYBAC Transposons for Sustained and Robust Liver-targeted Gene Therapy.(2014)
Authors: Mario Di Matteo, Ermira Samara, N. Ward, J. Mcvey
Pages: 1614-1624 - Liver-Specific Transcriptional Modules Identified by Genome-Wide in Silico Analysis Enable Efficient Gene Therapy in Mice and Non-Human Primates.(2014)
Authors: I. Petrus, P De Bleser, Caroline Le Guiner, G. Gernoux, O. Adjali, Nisha Nair, Jessica Willems, Hanneke Evens, M.y. Rincon, Janka Matrai, et al.
Pages: 1605-1613