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Publication
Quantifying benefit-risk preferences for new medicines in rare disease patients and caregivers
Journal Contribution - Journal Article
Rare disease patients and caregivers face uncommon, serious, debilitating conditions often characterised by poor prognosis and limited treatment options. This study aimed to explore what they consider of value when choosing between hypothetical therapeutic options and to quantify both their benefit-risk preferences and the influence of disease context.
Journal: Orphanet Journal of Rare Diseases
ISSN: 1750-1172
Issue: 70
Volume: 11
Publication year:2016