- Nanoblades allow high-level genome editing in murine and human organoids.(2023)
Auteurs: Mattijs Bulcaen, Marjolein Ensinck, Louise Medaer, Rik Gijsbers, Marianne Carlon
Pagina's: 57 - 74
- Functional restoration of a CFTR splicing mutation through RNA delivery of CRISPR adenine base editor(2023)
Auteurs: Marjolein Ensinck, Marianne Carlon
Pagina's: 1647 - 1660
- Development of novel therapeutic strategies for rare CFTR mutations causing severe cystic fibrosis(2023)
Auteurs: Marjolein Ensinck, Zeger Debyser, Christiane De Boeck, Marianne Carlon
- Base editing strategy to repair the CFTR 2789+5G > A splicing mutation(2022)
Auteurs: Marjolein Ensinck, François Vermeulen, Marianne Carlon
Pagina's: A137 - A137
- Nanoblades allow high-level genome editing in organoids(2022)
Auteurs: Mattijs Bulcaen, Marjolein Ensinck, Louise Medaer, Rik Gijsbers, Marianne Carlon
Pagina's: A8 - A8
- Severity of the S1251N allele in cystic fibrosis is affected by the presence of the F508C variant in cis(2022)
Auteurs: Senne Cuyx, Kaline Arnauts, Marc Ferrante, Catherine Verfaillie, Marjolein Ensinck, Marianne Carlon, Mieke Boon, Marijke Proesmans, Lieven Dupont, François Vermeulen
Pagina's: 644 - 651
- One Size Does Not Fit All: The Past, Present and Future of Cystic Fibrosis Causal Therapies(2022)
Auteurs: Marjolein Ensinck, Marianne Carlon
- Novel CFTR modulator combinations maximise rescue of G85E and N1303K in rectal organoids(2022)
Auteurs: Marjolein Ensinck, Senne Cuyx, Lieven Dupont, Frauke Christ, Zeger Debyser, François Vermeulen, Marianne Carlon
- On the Corner of Models and Cure: Gene Editing in Cystic Fibrosis(2021)
Auteurs: Marjolein Ensinck, Marianne Carlon
- Transcriptomic analysis of CFTR-impaired endothelial cells reveals a pro-inflammatory phenotype(2021)
Auteurs: Mathias Declercq, Vincent Geldhof, Marjolein Ensinck, Marianne Carlon, Matthew Bird, Marijke Proesmans, François Vermeulen, Lieven Dupont, Maria Dewerchin, Peter Carmeliet, et al.