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Onderzoeker
Marinee Chuah
- Disciplines:Cardiale en vasculaire geneeskunde, Moleculaire en celbiologie
Affiliaties
- Centrum voor Moleculaire en Vasculaire Biologie (Afdeling)
Lid
Vanaf1 okt 2000 → Heden
Projecten
1 - 2 of 2
- Ontwikkeling van stamcel-gentherapie voor Duchenne musculaire dystrofie.Vanaf27 sep 2010 → 16 jun 2016Financiering: FWO mandaten
- Rol van microRNA regulatie in de controle van hepatocarcinogenese: in vivo validatie, moleculaire mechanismen en therapeutische implicaties.Vanaf1 jan 2010 → 31 dec 2015Financiering: FWO Onderzoeksproject (incl. WEAVE projecten)
Publicaties
1 - 10 van 108
- Dose-Dependent Microdystrophin Expression Enhancement in Cardiac Muscle by a Cardiac-Specific Regulatory Element(2021)
Auteurs: Thierry Vandendriessche, Marinee Chuah
Pagina's: 1138 - 1146 - Next-generation muscle-directed gene therapy by in silico vector design(2019)
Auteurs: Emanuele Berardi, Maurilio Sampaolesi, Thierry Vandendriessche, Marinee Chuah
- Getting Into the Rhythm With CRISPR(2018)
Auteurs: Thierry Vandendriessche, Marinee Chuah
Pagina's: 928 - 930 - Efficient CRISPR/Cas9-mediated editing of trinucleotide repeat expansion in myotonic dystrophy patient-derived iPS and myogenic cells(2018)
Auteurs: Yoke Chin Chai, Joris Vermeesch, Marinee Chuah, Thierry Vandendriessche
Pagina's: 8275 - 8298 - A Calsequestrin Cis-Regulatory Motif Coupled to a Cardiac Troponin T Promoter Improves Cardiac Adeno-Associated Virus Serotype 9 Transduction Specificity(2018)
Auteurs: Thierry Vandendriessche, Marinee Chuah
Pagina's: 927 - 937 - Efficient In Vivo Liver-Directed Gene Editing Using CRISPR/Cas9(2018)
Auteurs: Marinee Chuah, Thierry Vandendriessche
Pagina's: 1241 - 1254 - Haemophilia gene therapy: From trailblazer to gamechanger(2018)
Auteurs: Marinee Chuah, Thierry Vandendriessche
Pagina's: 50 - 59 - Hyperactive Factor IX Padua: A Game-Changer for Hemophilia Gene Therapy(2018)
Auteurs: Thierry Vandendriessche, Marinee Chuah
Pagina's: 14 - 16 - Preclinical and clinical advances in transposon-based gene therapy(2017)
Auteurs: Yoke Chin Chai, Marinee Chuah
- CRISPR/Cas9-Mediated Editing of Trinucleotide Repeat Expansion in Myotonic Dystrophy(2017)
Auteurs: Sumitava Dastidar, Kshitiz Singh, Nisha Nair, Yanfang Fu, Deepak Reyon, Ermira Samara, Mattia FM Gerli, Arnaud F Klein, Thomas Jans, Jaitip Tipanee, et al.
Pagina's: 85 - 85
Patenten
1 - 1 van 1