Genetic therapy for EYS- and USH2A-associated retinal dystrophy ("GET-READY") Ghent University
Inherited retinal diseases (IRDs) are a group of disorders with a prevalence of approximately 1 in 3,000
people, accounting for about 200,000 patients within the European Union. Due to the complexity of the
visual system, several hundred proteins are uniquely expressed in the retina, and mutations in over 200
different genes are associated with IRD. Over the last decade, specific advantages of the eye have
positioned this ...