Hemophilia gene therapy knowledge and perceptions Vrije Universiteit Brussel
Background: Hemophilia gene therapy is a rapidly evolving therapeutic approach in which a number of programs are approaching clinical development completion.
Objective: The aim of this study was to evaluate knowledge and perceptions of a variety of health care practitioners and scientists about gene therapy for hemophilia.
Methods: This survey study was conducted February 1 to 18, 2019. Survey participants were members of the ...