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Publication
NEO1 AND NEO-EXT STUDIES: PHARMACODYNAMIC/EXPLORATORY BIOMARKER AND SAFETY ASSESSMENTS FOLLOWING REPEAT AVALGLUCOSIDASE ALFA DOSING FOR UP TO 4.5 YEARS IN PATIENTS WITH LATE-ONSET POMPE DISEASE
Journal Contribution - Journal Article Conference Contribution
Journal: MUSCLE & NERVE
ISSN: 0148-639X
Volume: 60
Pages: S48 - S49
Publication year:2019